Niemann-Pick Disease Type C Archives - The Children's Inn at NIH

Valley family fights for drug to save sick child

IJMS Special Issue : Advances in Knowledge in Niemann-Pick Disease Type C: Facts and Perspectives- 2nd Edition

Timeline – 2010-2017 - The Children's Inn at NIH

Institute of child health hi-res stock photography and images - Alamy

Timeline – 2010-2017 - The Children's Inn at NIH

Timeline – 2010-2017 - The Children's Inn at NIH

NIH teams with industry to develop treatments for Niemann-Pick Type C disease.

Timeline – 2010-2017 - The Children's Inn at NIH

TRIALS: A Fight for Children with Niemann-Pick Type C, a Fatal Genetic Disease

Niemann–Pick type C disease: cellular pathology and pharmacotherapy - Wheeler - 2020 - Journal of Neurochemistry - Wiley Online Library

Niemann-Pick disease type C clinical database: cognitive and coordination deficits are early disease indicators, Orphanet Journal of Rare Diseases