Adult Onset Niemann-Pick type C (NPC) – NNPDF
Por um escritor misterioso
Last updated 18 fevereiro 2025
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Defining Natural History: Assessment of the Ability of College Students to Aid in Characterizing Clinical Progression of Niemann-Pick Disease, Type C
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Investigational New Drug (IND) - The Addi and Cassi Fund
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Niemann-Pick disease type C, Orphanet Journal of Rare Diseases
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Adult onset Niemann-Pick disease type C presenting with psychosis
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IJMS, Free Full-Text
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Signatures of natural selection and ethnic-specific prevalence of NPC1 pathogenic mutations contributing to obesity and Niemann–Pick disease type C1
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Evaluation of age of death in Niemann-Pick disease, type C: Utility of disease support group websites to understand natural history - ScienceDirect
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PDF) The adult form of Niemann-Pick type C
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Blog – NNPDF
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Niemann-Pick disease type C
Defining Natural History: Assessment of the Ability of College Students to Aid in Characterizing Clinical Progression of Niemann-Pick Disease, Type C
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PDF) Niemann-Pick disease type C
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Correction of Niemann-Pick type C1 trafficking and activity with the histone deacetylase inhibitor valproic acid - Journal of Biological Chemistry
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Blog – NNPDF
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